MeiraGTx Reports Publication Of Results From First-in-human Interventional Study To Treat Children With AIPL1-Associated Severe Retinal Dystrophy
Author: Benzinga Newsdesk | February 21, 2025 06:32am
As disclosed in the paper, 4 out of 4 young children with the AIPL1-related retinal dystrophy, LCA4, benefited substantially from unilateral subretinal administration of rAAV8.hRKp.AIPL1 with improved visual acuity, functional vision, and protection against progressive retinal degeneration, the company said.
Posted In: MGTX